
Global Medical Director LC FAOD and MPS
Position Summary:
ultrafocused – Work together to fearlessly uncover new possibilities
Ultragenyx is seeking an experienced physician leader with a passion for rare and ultra-rare diseases. Reporting to the Global Medical Lead, the Director will be a key contributor to shaping the strategy and executing the medical affairs plans for LC-FAOD, MPS VII and MPS IIIA. This role offers a unique opportunity to be part of highly collaborative cross-functional teams working on both approved therapies (Dojolvi and Mepsevii), and an investigational AAV gene therapy (UX111) as we prepare for future potential launches.
Work Model:
Remote: Officially documented as working full-time from home, with travel to Ultragenyx's offices or other locations on occasion as needed.
Responsibilities:
- Provide strategic medical and scientific leadership to LC‑FAOD (Dojolvi) and the MPS programs (MPS VII and MPS IIIA) to support the development and execution of the global medical plans.
- Contribute to the development and execution of the annual Integrated Evidence Generation Plans.
- Provide medical expertise and leadership to Real‑World Evidence initiatives (e.g., ISTs, collaborative research) and the Disease Monitoring Programs for LC‑FAOD and MPS focused on data generation and publication activities.
- Act as a subject matter expert in assigned therapeutic areas, guiding and contributing to the execution of key global medical affairs activities including advisory boards, medical education initiatives and congress activities.
- Lead robust scientific engagement and education, maintaining strong relationships with external stakeholders to generate insights and advance scientific understanding of assigned programs.
- Provide scientific and medical leadership as needed for publication and medical communication material development.
- Serve as a medical reviewer for promotional materials and non-promotional scientific materials ensuring accuracy, balance, strategic alignment and compliance with regulatory requirements.
- Provide subject matter expertise to develop and deliver training across the organization.
- Collaborate cross‑functionally with Clinical Development, Commercial, Regulatory, HEOR, Biostatistics, Patient Advocacy, Regional Medical Teams and others to achieve program goals.
Requirements:
- Medical Doctor (MD or DO) required.
- Clinical expertise in the management of patients with inherited metabolic and/or neurodegenerative rare diseases strongly preferred.
- At least 2 years of experience in the pharmaceutical industry is preferred, but extensive relevant clinical experience may be considered as an alternative.
- Strategic thinker with strong execution discipline and a proven ability to manage multiple projects.
- Ability to interpret and communicate complex clinical and scientific information to a range of audiences.
- Highly analytical in approach to work, with the ability to identify interdependencies, consider the medical implications and understand the broader goals of a program and the organization.
- Ability to work independently and as a member of a cross-functional matrix team in a fast-paced environment.
- High attention to detail, demand for high-quality work, and sense of passion and urgency to achieve goals and improve the lives of patients.
- Willingness and ability to travel up to 15%, including domestic and international engagements.
#LI-AM1 #LI-Remote
The typical annual salary range for this full-time position is listed below. This range reflects the characteristics of the job, such as required skills and qualifications and is based on the office location noted in this job posting. The range may also be adjusted based on applicant's geographic location.
This position is eligible for annual bonus and equity incentives. Actual individual pay is determined by demonstrated experience and internal equity alignment.
Pay Range
$259,600 - $320,700 USD
Ultragenyx Pharmaceutical is an equal opportunity employer and prohibits unlawful discrimination based on race, color, religion, gender, sexual orientation, gender identity/expression, national origin/ancestry, age, disability, marital and veteran status, and any other status or classification protected by applicable federal, state, and/or local laws. Reasonable accommodation will be provided for all protected statuses or classifications protected by applicable law, including individuals with disabilities, disabled veterans, for pregnancy, childbirth, and related medical conditions, and based on sincerely held religious beliefs. Applicants can request an accommodation prior to accepting a job offer. If you require reasonable accommodation in completing this application, or in any part of the recruitment process, you may contact Talent Acquisition by emailing us at talentacquisition@ultragenyx.com.
It is unlawful in Massachusetts to require or administer a lie detector test as a condition of employment or continued employment. An employer who violates this law shall be subject to criminal penalties and civil liability.
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